Meet Maddie, the Children’s Mercy patient battling Angelman syndrome who exudes positivity

Angelman syndrome is a rare genetic disorder that impacts brain development, speech, movement, and learning.
ABC12

Montrose family raising money for 6-year-old boy with Angelman Syndrome

MONTROSE, Mich. (WJRT) - A Mid-Michigan family is raising money to help their 6-year-old boy with a rare genetic disorder. After spending a few months looking for action figures and fun items, Kristin ...
Cleveland.com

Local Westlake family helps raise funds for Angelman Syndrome research

The Pinball Lounge at 78th Street Sudios offers an ideal setting for this unique fundraiser. The event runs from 4-6 pm, providing families with an accessible Sunday afternoon activity. True to its ...
Hosted on MSN

What is Angelman Syndrome? As Colin Farrell makes plan for son James

Colin Farrell has opened up on his difficult decision to place his disabled son in long-term care. James was born to Colin and ex-partner US model Kim Bordenave. The youngster was diagnosed with the ...
Morningstar

MavriX Bio Receives FDA Fast Track Designation for MVX-220 for Treatment of Angelman Syndrome

MIDDLETON, Mass., Sept. 22, 2025 /PRNewswire/ -- MavriX Bio, a clinical-stage biotechnology company focused on the development of transformative genetic therapies for Angelman syndrome (AS), today ...
Nasdaq

Ultragenyx Pharmaceutical Inc. Doses First Patient in Pivotal Phase 3 Aspire Study for GTX-102 in Angelman Syndrome

Ultragenyx Pharmaceutical Inc. announced the dosing of the first patient in its Phase 3 Aspire study, which is investigating the safety and efficacy of GTX-102, an investigational antisense ...