In September last year, we reported Servier had advanced its emerging neurology pipeline into the clinical trials stage by ...

For 22 years, Jason Mazzola's life was defined by a genetic condition that can cause autism and intellectual disability. Then he started taking an... Fragile X held him back. An experimental drug is ...

The genetic disorder Fragile X syndrome occurs when individuals don't make the Fragile X protein known as FMRP. Essential for normal brain development, FMRP helps control when and where proteins are ...

Harmony Biosciences’ transdermal cannabidiol ZYN002 suffered a setback as a Phase III trial failed to meet the primary endpoint in a Fragile X Syndrome trial, with the biotech blaming a ...

Scientists have created a new therapeutic approach for testing fragile X syndrome, which is the most common genetic cause of autism spectrum disorder (ASD). This method aims to alter a type of neural ...

A new study suggests a potential molecular strategy for treating fragile X syndrome, an inherited neurodevelopmental disorder that causes autism spectrum disorder and intellectual disability. This ...

For individuals living with fragile X syndrome — a common genetic disorder that is correlated with autism, causes intellectual disability and more frequently affects male individuals — anxiety, ...

Numerous potential treatments for neurological conditions, including autism spectrum disorders, have worked well in lab mice but then disappointed in humans. What would help is a non-invasive, ...

For 22 years, Jason Mazzola’s life was defined by Fragile X, a genetic condition that often causes autism and intellectual disability. Jason, who is 24 now, needed constant supervision. He had ...